rette syndrome

by Nadine A Yehya, UC Davis edited by Stephanie Baum, reviewed by Andrew Zinin  A CRISPR/Cas9 screen identifies miRNAs as regulators of mammalian XCI. Credit: Nature Communications (2025). DOI: 10.1038/s41467-025-61092-7 Researchers led by UC Davis Health scientist Sanchita Bhatnagar have developed a promising gene therapy that could treat Rett syndrome. The therapy works on reactivating healthy but silent genes responsible […]

AI-enabled drug discovery approach identified potentially game-changing treatment which has been advanced from the lab bench to an FDA Orphan Drug Designation in record time Peer-Reviewed Publication Wyss Institute for Biologically Inspired Engineering at Harvard FacebookXLinkedInWeChatBlueskyMessageWhatsAppEmail image: This image shows a tadpole preparation which was stained for acetylated a-tubulin protein view more  Credit: Wyss Institute at Harvard University