Gene Therapy

Gene therapy may cure diabetic heart disease, mouse study shows

by Nature Publishing Group edited by Lisa Lock, reviewed by Robert Egan Editors’ notes A hypothetical mechanism of the glycophagy role in physiology and pathology involvement in diabetic heart disease. Credit: Nature Cardiovascular Research (2025). DOI: 10.1038/s44161-025-00726-x Scientists have reversed diabetic heart failure with a genetic therapy in mice and miniature human “hearts” grown from stem cells. The new gene […]

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Cell therapy prevents damage from Duchenne muscular dystrophy in mouse model

August 5, 2025 / Gene Therapy, Research update / InnovateMed Author / Duchenne Muscular Dystrophy

by Cedars-Sinai Medical Center edited by Lisa Lock, reviewed by Robert Egan Protection against functional decline in mdx mice by repeated CDC therapy. Credit: Stem Cell Reports (2025). DOI: 10.1016/j.stemcr.2025.102468 A cell therapy preserves muscle structure and function in laboratory mice with a type of disease similar to Duchenne muscular dystrophy, according to new research from the Smidt Heart Institute

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‘One and done’: A single shot at birth may shield children from HIV for years

July 31, 2025 / Clinical Practice, Gene Therapy / InnovateMed Author / HIV, HIV therapy for infants

by Tulane University edited by Gaby Clark, reviewed by Robert Egan Credit: Unsplash/CC0 Public Domain A new study in Nature shows that delivering a single injection of gene therapy at birth may offer years-long protection against HIV, tapping into a critical window in early life that could reshape the fight against pediatric infections in high-risk regions. This study is among the first

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Progress in gene therapy offers hope for long-term knee pain relief

July 30, 2025 / Gene Therapy, Genetics, Research update / InnovateMed Author / knee pain

edited by Sadie Harley, reviewed by Andrew Zinin Credit: Towfiqu barbhuiya from Pexels For nearly three decades, Mayo Clinic researcher Christopher Evans, Ph.D., has pushed to expand gene therapy beyond its original scope of fixing rare, single-gene defects. That has meant systematically advancing the field through laboratory experiments, pre-clinical studies and clinical trials. Several gene therapies have

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Gene therapy may cure diabetic heart disease, mouse study shows

Cell therapy prevents damage from Duchenne muscular dystrophy in mouse model

‘One and done’: A single shot at birth may shield children from HIV for years

Progress in gene therapy offers hope for long-term knee pain relief

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